Clinical efficacy of nusinersen in treating presymptomatic 5q spinal muscular atrophy: a case report and literature review

LUO Zhiqiang, LU Xinguo, LIU Liqin, LIAO Jianxiang

Journal of Clinical Pediatrics . 2022, (3): 208 -211 . DOI: 10.12372/jcp.2022.21e1539