Advances in real-world research on disease-modifying treatments for spinal muscular atrophy
WU Xian, LIU Yan, LIU Xinzhu, HUANG Xiaohui, MA Jing, XU A-jing, XIN Xiaodong, JIANG Wengao, ZHANG Jian
Journal of Clinical Pediatrics . 2025, (1): 61 -69 .  DOI: 10.12372/jcp.2025.23e0998