Efficacy and safety of nusinersen in spinal muscular atrophy patients with scoliosis
LIU Xinzhu, XING Xiaodong, LIU Yu, LIU Yan, JIANG Wengao, ZHANG Jian, YANG Junlin
Journal of Clinical Pediatrics . 2025, (10): 727 -733 .  DOI: 10.12372/jcp.2025.24e1128