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中文
Efficacy and safety of nusinersen in spinal muscular atrophy patients with scoliosis
LIU Xinzhu, XING Xiaodong, LIU Yu, LIU Yan, JIANG Wengao, ZHANG Jian, YANG Junlin
Journal of Clinical Pediatrics . 2025, (
10
): 727 -733 . DOI: 10.12372/jcp.2025.24e1128