Clinical phenotypes, genetic analysis and allogeneic hematopoietic stem cell transplantation efficacy of 8 children with metachromatic leukodystrophy
HU Jiayue, YING Lingwen, CHANG Guoying, LI Juan, YANG Fan, WANG Cuijin, YU Tingting, YAO Ruen, LUO Chengjuan, Wang Xiumin
Journal of Clinical Pediatrics
.
2025, (10): 734
-741
.
DOI: 10.12372/jcp.2025.25e0117
