诺西那生钠治疗脊柱侧凸脊髓性肌萎缩症患者的疗效及安全性研究
刘昕竹, 幸小东, 刘宇, 刘艳, 蒋文高, 张健, 杨军林
Efficacy and safety of nusinersen in spinal muscular atrophy patients with scoliosis
LIU Xinzhu, XING Xiaodong, LIU Yu, LIU Yan, JIANG Wengao, ZHANG Jian, YANG Junlin
临床儿科杂志
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2025, (10): 727
-733
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DOI: 10.12372/jcp.2025.24e1128